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Gene therapy trial for Huntington’s disease under way in Oxford

Clinical Trials General Research

Nuffield Department of Clinical Neuroscience’s Associate Professor Andrea Nemeth is leading the Oxford part of a gene therapy trial for Hungtinton’s disease.

Gene therapy trial for Huntington’s disease under way in Oxford © Oxford University Hospitals NHS Foundation Trust

This international collaborative trial, sponsored by Roche pharmaceuticals, is the first gene therapy trial for a neurodegenerative disease of the central nervous system. If successful, the trial could have implications not just for Huntington’s disease but also genetically similar conditions such as the spinocerebellar ataxias.

Read more (Nuffield Department of Clinical Neuroscience website)

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